【レポートの概要（一部）】
Table of Contents
Table of Contents 2
List of Tables 4
List of Figures 4
Introduction 5
Global Markets Direct Report Coverage 5
Inclusion Body Myositis (IBM) Overview 6
Therapeutics Development 7
Pipeline Products for Inclusion Body Myositis (IBM) – Overview 7
Pipeline Products for Inclusion Body Myositis (IBM) – Comparative Analysis 8
Inclusion Body Myositis (IBM) – Therapeutics under Development by Companies 9
Inclusion Body Myositis (IBM) – Pipeline Products Glance 10
Late Stage Products 10
Clinical Stage Products 11
Inclusion Body Myositis (IBM) – Products under Development by Companies 12
Inclusion Body Myositis (IBM) – Companies Involved in Therapeutics Development 13
Acceleron Pharma, Inc. 13
New Zealand Pharmaceuticals Limited 14
Nobelpharma Co., Ltd. 15
Novartis AG 16
Ultragenyx Pharmaceutical Inc. 17
Inclusion Body Myositis (IBM) – Therapeutics Assessment 18
Assessment by Monotherapy Products 18
Assessment by Target 19
Assessment by Mechanism of Action 21
Assessment by Route of Administration 23
Assessment by Molecule Type 25
Drug Profiles 27
AAV1-Foliistatin – Drug Profile 27
Product Description 27
Mechanism of Action 27
R&D Progress 27
ACE-083 – Drug Profile 28
Product Description 28
Mechanism of Action 28
R&D Progress 28
aceneuramic acid – Drug Profile 29
Product Description 29
Mechanism of Action 29
R&D Progress 29
bimagrumab – Drug Profile 31
Product Description 31
Mechanism of Action 31
R&D Progress 31
DEXM-74 – Drug Profile 33
Product Description 33
Mechanism of Action 33
R&D Progress 33
UX-007 – Drug Profile 35
Product Description 35
Mechanism of Action 35
R&D Progress 35
Inclusion Body Myositis (IBM) – Recent Pipeline Updates 36
Inclusion Body Myositis (IBM) – Dormant Projects 43
Inclusion Body Myositis (IBM) – Product Development Milestones 44
Featured News & Press Releases 44
Jan 12, 2015: Ultragenyx Announces Intent to File for Conditional Approval in Europe for Sialic Acid Extended-Release Tablets in Hereditary Inclusion Body Myopathy 44
Oct 13, 2014: Ultragenyx Announces Interim Data From Phase 2 Extension Study of Sialic Acid Extended-Release at International Congress of the World Muscle Society 45
Apr 30, 2014: Ultragenyx Announces Positive Data From Phase 2 Study of Sialic Acid Extended-Release at Emerging Sciences Session of American Academy of Neurology Annual Meeting 45
Dec 20, 2013: Ultragenyx Announces Results from Phase 2 Study of Sialic Acid Extended-Release Treatment in Hereditary Inclusion Body Myopathy 47
Oct 02, 2013: MorphoSys Collaborator to Start Pivotal Study with Bimagrumab 47
Sep 26, 2013: Ultragenyx Announces Three Abstracts Accepted for Poster Presentation at 18th Annual World Muscle Society Congress 48
Aug 20, 2013: Novartis receives FDA breakthrough therapy designation for BYM338 (bimagrumab) for sporadic inclusion body myositis (sIBM) 48
Jul 03, 2013: Ultragenyx Announces a Positive Signal in Interim Data from Phase 2 Study of UX001 in Hereditary Inclusion Body Myopathy 49
Dec 15, 2011: New Zealand Pharma Obtains FDA Orphan Drug Designation For DEX-M74 To Treat Hereditary Inclusion Body Myopathy 50
Appendix 51
Methodology 51
Coverage 51
Secondary Research 51
Primary Research 51
Expert Panel Validation 51
Contact Us 51
Disclaimer 52
【レポート販売概要】
■ タイトル：封入体筋炎(Inclusion Body Myositis (IBM))：治療薬開発パイプライン動向（2015年上半期版）■ 英文：Inclusion Body Myositis (IBM) - Pipeline Review, H1 2015
■ 発行日：2015年3月19日
■ 調査会社：Global Markets Direct
■ 商品コード：GMDHC6461IDB
■ 調査対象地域：グローバル
- 世界の木材・プラスチック複合材市場動向（2014-2018）About Wood-Plastics Composites Wood-plastic composites are materials, which hare made up of wood flour or fiber and plastic resins. These composites also contain a certain degree of additives, which foster the integration of the wood and plastic and aid in the manufacturing process. Most wood-plastic composites are manufactured using wood and plastic wastes or recyclates. A minor share of these pr …
- 世界におけるGPS/GNSS市場2013-2023（市場規模及び動因）Synopsis This report provides readers with a comprehensive analysis of the Military GPS/GNSS market through 2013 - 2023, including highlights of the demand drivers and growth stimulators for Military GPS/GNSS. It also provides an insight on the spending pattern and modernization pattern in different regions around the world. Summary The global GPS/GNSS devices market which values US$1.2 billion in …
- 自動車ワイヤーハーネスの世界市場予測（～2025年）“Rising trend of integrating advanced features for improving performance and driving experience and the increasing vehicle production are likely to fuel the demand for automotive wiring harness market”The automotive wiring harness market is estimated to be USD 81.17 billion in 2018 and is projected to grow at a CAGR of 5.83% during the forecast period, to reach a market size of USD 120.69 billion …
- 世界のSoftware Defined Data Center (SDDC) 市場Increasing use of internet and networking globally has significantly augmented the demand for more storage space, computing power and complex networking. This demand has given rise to scaling up of infrastructure in the existing data centers, thus increasing the capital expenditure and operating expenditure for data centers and the enterprises. This scaling up has also increased the complexity in …
- World Point Terminals Inc.：石油・ガスバリューチェーン分析レポート2013World Point Terminals Inc. Analysis Across the Oil and Gas Value Chain Report, 2013 Update Summary "World Point Terminals Inc." Analysis Across the Oil and Gas Value Chain is an essential source for data, analysis and strategic insight into “World Point Terminals Inc.”. The report provides key information relating to oil and gas assets of the company along with its operations across the value chai …
- Urinary Retention：グローバル臨床試験レビューH2, 2013Urinary Retention Global Clinical Trials Review, H2, 2013 Summary GlobalData's clinical trial report, “Urinary Retention Global Clinical Trials Review, H2, 2013" provides data on the Urinary Retention clinical trial scenario. This report provides elemental information and data relating to the clinical trials on Urinary Retention. It includes an overview of the trial numbers and their recruitment s …
- Dorchester Minerals, L.P.：石油・ガスの開発・生産動向及びコスト分析- Q2, 2013Dorchester Minerals, L.P. Oil & Gas Exploration and Production Operations and Cost Analysis - Q2, 2013 Summary Dorchester Minerals, L.P. Oil & Gas Exploration and Production Operations and Cost Analysis is the latest report from GlobalData, the industry analysis specialists, that offers comprehensive information on the operational and financial performance of the company. The report is an essentia …
- 放射線治療の世界市場：外部ビーム放射線療法、内部ビーム放射線療法、近接照射療法、全身放射線療法The radiotherapy market is expected to reach USD 7,544.8 Million by 2020 from USD 5,585.0 Million in 2015, at a CAGR of 6.2% between 2015 and 2020. A strong trend of increasing incidence of cancer cases across the globe majorly drives the growth of the market. Other growth factors include technological advancements in radiotherapy products, increasing symposiums driving investments in radiotherapy …
- ガーダシル（Gardasil/ヒトパピローマウイルスワクチン）：市場予測と分析（～2022）Gardasil (Prophylactic Human PapillomaVirus Vaccines) - Forecast and Market Analysis to 2022 Summary The first prophylactic vaccine for immunization against human papillomavirus (HPV) became available in 2006. The global HPV vaccines market is now well established, yet vaccine coverage rates amongst the traditional target population of adolescent girls remain persistently low. Initially HPV vaccin …
- 業務用サービスロボットの世界市場の世界市場Professional service robots have the tendency to work closely with humans and can be used in a wide application ranging from surveillance to underwater inspection. They provide convenience and safety, among other benefits, thus creating demand worldwide. Technavio expects the global professional service robotics market to multiply at a remarkable rate of nearly 16% during the forecast period. Toda …
- 世界の火力発電所用復水器（Steam Condenser）市場（2012-2016）TechNavio’s analysts forecast the Global Steam Condenser market for Thermal Power Plant to grow at a CAGR of 6.25 percent over the period 2012-2016. One of the key factors contributing to this market growth is the increased electricity consumption. The Global Steam Condenser market for Thermal Power Plant has also been witnessing the development of Clean Coal Technology (CCT). However, the increas …
- エンタープライズコンテンツ管理（ECM）の世界市場：文書管理、ウェブコンテンツ管理、記録管理、eDiscoveryToday, most of enterprises are vying to effectively address the voluminous amount of content being generated on a daily basis. This content may vary from spreadsheets to huge databases and can be highly unstructured. This huge chunk of content is defined as a goldmine of information to derive policies and align enterprises’ strategic initiatives. The enterprise content management market can be def …
- ICT予算及び人員配置動向：銀行部門 – 企業のICT投資計画Why was the report written? In order to provide a depth of insight into ICT vendors’ and service providers’ potential customers. What is the current market landscape and what is changing? ICT expenditure is a significant portion of operational spending in the retail banking industry. With business process streamlining a key priority, retail banks are increasing their ICT spending to improve their …
- アプリケーションセキュリティの世界市場2019-2023About this market The vendors in the market are offering cloud-based application security solutions to leverage the growing demand. Cloud-based solutions are less expensive than on-premises solutions. They do not require the actual installation of hardware and software, as they are maintained at the vendor's data center from where they can be accessed by enterprises on a subscription basis. Thus, …
- 未熟児網膜症(Retinopathy Of Prematurity)：世界の治験レビュー2014年下半期版Retinopathy Of Prematurity Global Clinical Trials Review, H2, 2014 Summary GlobalData's clinical trial report, “Retinopathy Of Prematurity Global Clinical Trials Review, H2, 2014" provides data on the Retinopathy Of Prematurity clinical trial scenario. This report provides elemental information and data relating to the clinical trials on Retinopathy Of Prematurity. It includes an overview of the t …
