【レポートの概要（一部）】
Table of Contents
Table of Contents 2
List of Tables 4
List of Figures 4
Introduction 5
Global Markets Direct Report Coverage 5
Atypical Hemolytic Uremic Syndrome (Nondiarrhea- Associated Hemolytic Uremic Syndrome) Overview 6
Therapeutics Development 7
Pipeline Products for Atypical Hemolytic Uremic Syndrome (Nondiarrhea- Associated Hemolytic Uremic Syndrome) – Overview 7
Pipeline Products for Atypical Hemolytic Uremic Syndrome (Nondiarrhea- Associated Hemolytic Uremic Syndrome) – Comparative Analysis 8
Atypical Hemolytic Uremic Syndrome (Nondiarrhea- Associated Hemolytic Uremic Syndrome) – Therapeutics under Development by Companies 9
Atypical Hemolytic Uremic Syndrome (Nondiarrhea- Associated Hemolytic Uremic Syndrome) – Pipeline Products Glance 10
Clinical Stage Products 10
Early Stage Products 11
Atypical Hemolytic Uremic Syndrome (Nondiarrhea- Associated Hemolytic Uremic Syndrome) – Products under Development by Companies 12
Atypical Hemolytic Uremic Syndrome (Nondiarrhea- Associated Hemolytic Uremic Syndrome) – Companies Involved in Therapeutics Development 13
Adienne Pharma & Biotech 13
Alnylam Pharmaceuticals, Inc. 14
ChemoCentryx, Inc. 15
Omeros Corporation 16
Atypical Hemolytic Uremic Syndrome (Nondiarrhea- Associated Hemolytic Uremic Syndrome) – Therapeutics Assessment 17
Assessment by Monotherapy Products 17
Assessment by Target 18
Assessment by Mechanism of Action 20
Assessment by Route of Administration 22
Assessment by Molecule Type 24
Drug Profiles 26
ALN-CC5 – Drug Profile 26
Product Description 26
Mechanism of Action 26
R&D Progress 26
CCX-168 – Drug Profile 27
Product Description 27
Mechanism of Action 27
R&D Progress 27
ET-006 – Drug Profile 29
Product Description 29
Mechanism of Action 29
R&D Progress 29
ETR-001 – Drug Profile 30
Product Description 30
Mechanism of Action 30
R&D Progress 30
Mubodina – Drug Profile 31
Product Description 31
Mechanism of Action 31
R&D Progress 31
OMS-721 – Drug Profile 32
Product Description 32
Mechanism of Action 32
R&D Progress 32
Atypical Hemolytic Uremic Syndrome (Nondiarrhea- Associated Hemolytic Uremic Syndrome) – Recent Pipeline Updates 34
Atypical Hemolytic Uremic Syndrome (Nondiarrhea- Associated Hemolytic Uremic Syndrome) – Dormant Projects 41
Atypical Hemolytic Uremic Syndrome (Nondiarrhea- Associated Hemolytic Uremic Syndrome) – Product Development Milestones 42
Featured News & Press Releases 42
Nov 20, 2014: ChemoCentryx’s CCX168, an Orally Administered Complement C5a Receptor Inhibitor, Granted Orphan-Drug Designation in Atypical Hemolytic Uremic Syndrome Treatment by the FDA 42
Nov 19, 2014: OMS721 Inhibits Thrombus Formation in Sera from aHUS Patients 42
Apr 03, 2014: Investigational New Drug Application Cleared by FDA for OMS721 in Thrombotic Microangiopathies 43
Mar 10, 2014: Omeros Announces Positive OMS721 Data in Serum from Patients with aHUS 44
Mar 04, 2014: Omeros Submits IND to Advance OMS721 Phase 2 Clinical Program 45
Feb 03, 2014: Omeros Announces Positive Data after Completion of Dosing in Phase 1 Clinical Trial with OMS721 47
Dec 18, 2013: FDA Grants Orphan Drug Designation to Omeros’ OMS721 for Complement-Mediated Thrombotic Microangiopathies 47
Jun 20, 2013: Alnylam Scientists Present Preclinical Data With ALN-CC5 For Treatment Of Complement-mediated Diseases 48
Jun 13, 2013: Omeros Obtains Regulatory Approval To Initiate Phase I Clinical Trial For Lead Antibody In MASP-2 Program 50
May 28, 2013: Omeros Files Clinical Trial Application For Lead Antibody In MASP-2 Program 51
Appendix 53
Methodology 53
Coverage 53
Secondary Research 53
Primary Research 53
Expert Panel Validation 53
Contact Us 54
Disclaimer 54
【レポート販売概要】
■ タイトル：非定型溶血性尿毒症症候群(Atypical Hemolytic Uremic Syndrome)の治療薬パイプライン動向（2015年上半期版）■ 英文：Atypical Hemolytic Uremic Syndrome (Nondiarrhea- Associated Hemolytic Uremic Syndrome) - Pipeline Review, H1 2015
■ 発行日：2015年1月22日
■ 調査会社：Global Markets Direct
■ 商品コード：GMDHC6106IDB
■ 調査対象地域：グローバル
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- モバイル衛星サービス（MSS）の世界市場2016-2020About Mobile Satellite Services Mobile satellite services (MSS) provide effective communication services beyond the terrestrial range and serves as an ultimate and appropriate channel in emergency situations. MSS include voice, low-speed data, fax, paging, high-speed data, and broadcast and video on demand. MSS systems are categorized based on their orbital altitudes such as geostationary orbit (G …
- 充血（Hyperemia）：治療薬のグローバル治験動向（2014年下半期）Hyperemia Global Clinical Trials Review, H2, 2014 Summary GlobalData's clinical trial report, “Hyperemia Global Clinical Trials Review, H2, 2014" provides data on the Hyperemia clinical trial scenario. This report provides elemental information and data relating to the clinical trials on Hyperemia. It includes an overview of the trial numbers and their recruitment status as per the site of trial c …
- スマート水管理ソリューションの世界市場：先進水道メーター、ネットワークモニタリング、圧力管理、分析、メーターデータ管理The Smart Water Management (SWM) market has witnessed a major growth over recent years with the integration of ICT in different verticals, and increasing adoption of technologies. This has helped in proper water management and reduction of Non-Revenue Water (NRW) loss due to leaks, thefts, pipe bursts, and metering errors. With the increasing demand of SWM solutions, key players are also investing …
- 米州のテニスウェア市場2016-2020About the Tennis Apparel Market in the Americas The tennis apparel market in the Americas is driven by a number of growth factors — one of the most important being the increasing number of tennis tournaments being organized and played across the region. The growing interest in tennis and the increasing participation of children will also have a positive influence on the growth of the market over t …
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