【レポートの概要（一部）】
Table of Contents
Table of Contents 2
List of Tables 4
List of Figures 4
Introduction 5
Global Markets Direct Report Coverage 5
Inclusion Body Myositis (IBM) Overview 6
Therapeutics Development 7
Pipeline Products for Inclusion Body Myositis (IBM) – Overview 7
Pipeline Products for Inclusion Body Myositis (IBM) – Comparative Analysis 8
Inclusion Body Myositis (IBM) – Therapeutics under Development by Companies 9
Inclusion Body Myositis (IBM) – Pipeline Products Glance 10
Late Stage Products 10
Clinical Stage Products 11
Inclusion Body Myositis (IBM) – Products under Development by Companies 12
Inclusion Body Myositis (IBM) – Companies Involved in Therapeutics Development 13
Acceleron Pharma, Inc. 13
New Zealand Pharmaceuticals Limited 14
Nobelpharma Co., Ltd. 15
Novartis AG 16
Ultragenyx Pharmaceutical Inc. 17
Inclusion Body Myositis (IBM) – Therapeutics Assessment 18
Assessment by Monotherapy Products 18
Assessment by Target 19
Assessment by Mechanism of Action 21
Assessment by Route of Administration 23
Assessment by Molecule Type 25
Drug Profiles 27
AAV1-Foliistatin – Drug Profile 27
Product Description 27
Mechanism of Action 27
R&D Progress 27
ACE-083 – Drug Profile 28
Product Description 28
Mechanism of Action 28
R&D Progress 28
aceneuramic acid – Drug Profile 29
Product Description 29
Mechanism of Action 29
R&D Progress 29
bimagrumab – Drug Profile 31
Product Description 31
Mechanism of Action 31
R&D Progress 31
DEXM-74 – Drug Profile 33
Product Description 33
Mechanism of Action 33
R&D Progress 33
UX-007 – Drug Profile 35
Product Description 35
Mechanism of Action 35
R&D Progress 35
Inclusion Body Myositis (IBM) – Recent Pipeline Updates 36
Inclusion Body Myositis (IBM) – Dormant Projects 43
Inclusion Body Myositis (IBM) – Product Development Milestones 44
Featured News & Press Releases 44
Jan 12, 2015: Ultragenyx Announces Intent to File for Conditional Approval in Europe for Sialic Acid Extended-Release Tablets in Hereditary Inclusion Body Myopathy 44
Oct 13, 2014: Ultragenyx Announces Interim Data From Phase 2 Extension Study of Sialic Acid Extended-Release at International Congress of the World Muscle Society 45
Apr 30, 2014: Ultragenyx Announces Positive Data From Phase 2 Study of Sialic Acid Extended-Release at Emerging Sciences Session of American Academy of Neurology Annual Meeting 45
Dec 20, 2013: Ultragenyx Announces Results from Phase 2 Study of Sialic Acid Extended-Release Treatment in Hereditary Inclusion Body Myopathy 47
Oct 02, 2013: MorphoSys Collaborator to Start Pivotal Study with Bimagrumab 47
Sep 26, 2013: Ultragenyx Announces Three Abstracts Accepted for Poster Presentation at 18th Annual World Muscle Society Congress 48
Aug 20, 2013: Novartis receives FDA breakthrough therapy designation for BYM338 (bimagrumab) for sporadic inclusion body myositis (sIBM) 48
Jul 03, 2013: Ultragenyx Announces a Positive Signal in Interim Data from Phase 2 Study of UX001 in Hereditary Inclusion Body Myopathy 49
Dec 15, 2011: New Zealand Pharma Obtains FDA Orphan Drug Designation For DEX-M74 To Treat Hereditary Inclusion Body Myopathy 50
Appendix 51
Methodology 51
Coverage 51
Secondary Research 51
Primary Research 51
Expert Panel Validation 51
Contact Us 51
Disclaimer 52
【レポート販売概要】
■ タイトル：封入体筋炎(Inclusion Body Myositis (IBM))：治療薬開発パイプライン動向（2015年上半期版）■ 英文：Inclusion Body Myositis (IBM) - Pipeline Review, H1 2015
■ 発行日：2015年3月19日
■ 調査会社：Global Markets Direct
■ 商品コード：GMDHC6461IDB
■ 調査対象地域：グローバル
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- Child Abuse：グローバル臨床試験レビューH2, 2013Child Abuse Global Clinical Trials Review, H2, 2013 Summary GlobalData's clinical trial report, “Child Abuse Global Clinical Trials Review, H2, 2013" provides data on the Child Abuse clinical trial scenario. This report provides elemental information and data relating to the clinical trials on Child Abuse. It includes an overview of the trial numbers and their recruitment status as per the site of …
- ロシアの心臓律動管理（CRM）装置市場見通しRussia Cardiac Rhythm Management (CRM) Procedures Outlook to 2021 Summary GlobalData’s new report, "Russia Cardiac Rhythm Management (CRM) Procedures Outlook to 2021", provides key procedures data on the Russia Cardiac Rhythm Management (CRM) Procedures. The report provides procedure volumes within market segments - Implantable Loop Recorder (ILR) Procedures, Cardiac Resynchronisation Therapy (CRT …
- ゲルコートの世界市場：ポリエステル樹脂、ビニルエステル樹脂、エポキシ樹脂The global demand for gelcoats is projected to reach USD 1,233 Million by 2020, registering a CAGR of 7.60% between 2015 and 2020. The growing composite usage in various industries, recovery of marine industry after the economic recession, and increase in demand for gelcoats in the transportation industry are the major factors driving the growth of the gelcoats market. The key resin types covered …
- 低光量イメージングの世界市場予測（～2024年）Increasing penetration of low-light image sensing technology in smartphones and the growing popularity of CMOS technology drives market growth The low-light imaging market is expected to grow at a CAGR of 12.8% from 2019 to 2024, to reach USD 18.4 billion by 2024 from USD 10.0 billion in 2019. Increasing penetration of low-light image sensors in smartphones and the growing popularity of CMOS techn …
- 核医学イメージング装置の世界市場：PET、SPECTAbout Nuclear Imaging Nuclear imaging is a non-invasive procedure used to diagnose and treat various diseases such as cancer, heart diseases, and brain disorders. In this procedure, radioactive substances are used to provide a detailed image of the body at the molecular as well as the cellular level. A small amount of the radioactive particle is taken internally, orally or intravenously. External …
- 世界主要先進国におけるてんかん治療薬市場動向（～2019）Epilepsy Therapeutics in Major Developed Markets to 2019 - New AEDs with Novel Mechanisms of Action Signal a Shift in Treatment Patterns Summary GBI Research has released its pharma research, "Epilepsy Therapeutics in Major Developed Markets to 2019 - New AEDs with Novel Mechanisms of Action Signal a Shift in Treatment Patterns", which provides in-depth analysis of epilepsy market within the eight …
